Severe combined immunodeficiency… what’s that? It doesn’t sound too good.

严重联合免疫缺陷… … 那是什么？听起来不太好。

It's becoming a reality to correct defective genes in patients with inherited diseases, such as severe combined immunodeficiency, you may know it as the bubble boy syndrome, and sickle cell anemia.

纠正遗传性疾病患者的缺陷基因正在成为现实，例如严重的联合免疫缺陷， 你可能知道它是泡泡男孩综合症和镰状细胞性贫血。